Researchers sought to determine whether there is a need for regular kidney surveillance to detect dysfunction among pediatric patients with transfusion-dependent thalassemia.
Τhe COVID-19 pandemic has exacerbated challenges in thalassemia care worldwide.
Researchers sought to determine whether the COVID-19 mRNA vaccines were safe and effective in patients with transfusion-dependent beta-thalassemia.
Researchers sought to determine whether luspatercept would improve outcomes in patients with nontransfusion-dependent β-thalassemia.
The application is supported by data from the phase 2 BEYOND study.
Researchers sought to determine whether a droplet digital PCR would be effective for noninvasive prenatal diagnosis of thalassemia.
Researchers sought to determine the clinical outcomes of children with thalassemia whose parents did or did not undergo prenatal diagnosis testing.
Researchers sought to determine whether patients with beta thalassemia heterozygosity are at higher risk of morbidity and mortality from COVID-19.
Researchers sought to determine a correlation between endocrine levels and iron overload in patients with transfusion-dependent beta thalassemia and growth retardation.
Researchers sought to review the EU’s marketing authorization for luspatercept to treat select patients with MDS or transfusion-dependent beta thalassemia.
