Researchers sought to determine the clinical outcomes of children with thalassemia whose parents did or did not undergo prenatal diagnosis testing.
Researchers sought to determine whether patients with beta thalassemia heterozygosity are at higher risk of morbidity and mortality from COVID-19.
Researchers sought to determine a correlation between endocrine levels and iron overload in patients with transfusion-dependent beta thalassemia and growth retardation.
Researchers sought to review the EU’s marketing authorization for luspatercept to treat select patients with MDS or transfusion-dependent beta thalassemia.
Researchers sought to determine whether patients with thalassemia may have growth impairments from their disease.
Researchers sought to conduct an economic evaluation of the use of beti-cel gene therapy in the treatment of transfusion-dependent -thalassemia.
Researchers sought to determine whether MRI T2 is an effective way to detect iron concentrations in the heart, liver, and pancreas during chelation therapy for patients with thalassemia major.
Researchers sought to determine whether carvedilol would improve left ventricular diastolic function in patients with transfusion‑dependent thalassemia who had iron overload cardiomyopathy.
Researchers sought to determine whether mitapivat would improve clinical outcomes in patients with thalassemias who are not transfusion-dependent.
Researchers sought to validate the usefulness of cardiac T2* magnetic resonance imaging to evaluate cardiac siderosis in patients with thalassemia major.
