In Utero Transfusions Support Improved Survival in Patients With Alpha Thalassemia Major
Researchers sought to determine whether in utero transfusions would yield improved survival for patients with alpha thalassemia major.
Researchers sought to determine whether in utero transfusions would yield improved survival for patients with alpha thalassemia major.
Researchers sought to determine whether there was a relationship between hepatocyte transferrin receptor 1 and iron homeostasis.
Researchers sought to determine whether hydroxyurea with thalidomide would improve hemoglobin levels in pediatric patients with beta-thalassemia.
Researchers sought to determine whether vitamin D deficiency before hematopoietic stem cell transplantation would impact risk of GVHD in thalassemia major.
Researchers sought to determine whether longitudinal strain with conventional TTE parameters could identify subclinical myocardial dysfunction associated with iron overload in thalassemia.
Researchers sought to determine whether treatment with betibeglogene autotemcel could improve QoL in patients with transfusion-dependent beta-thalassemia.
Researchers investigated a novel beta-thalassemia deletion that removes the entire beta-globin gene.
Researchers sought to determine the utility of HSCT in patients with beta-thalassemia and SCD with recurrent vaso-occlusive crises.
Researchers sought to determine whether including LGE in CMR-based evaluations of iron-induced heart failure could improve prognostic stratification in thalassemia major.
Researchers sought to determine whether mitapivat would be safe and effective in patients with alpha- or beta-NTDT.