Hemophilia

Researchers sought to determine whether emicizumab would be effective in treating pediatric patients with hemophilia A.

Researchers sought to determine whether gene therapy FLT180a would improve factor IX levels in patients with hemophilia B.

Researchers sought to determine whether there were improvements in joint health in patients with hemophilia A taking emicizumab prophylaxis therapy.

Researchers compared a consumer-grade activity monitor and a research-grade accelerometer for measuring activity in patients with hemophilia.

Researchers sought to improve the understanding of hemophilia by conducting a wide-scale genotype analysis for patients in the United States.

Researchers sought to determine the clinical and financial burden of patients with severe hemophilia A.

Researchers sought to determine whether extended half-life recombinant factor VIII would lead to a lower ABR in pediatric patients with severe hemophilia A.