New Study Evaluating BPA Use With Emicizumab Among Patients With Hemophilia A
Researchers are seeking to evaluate outcomes after initiation of emicizumab and concomitant BPAs in patients with hemophilia A and FVIII inhibitors.
Bleeding Disorders
Emicizumab Safe, Effective in Patients With Hemophilia A With FVIII Inhibitors
Researchers sought to determine whether emicizumab would be safe and effective in pediatric patients with hemophilia A with FVIII inhibitors.
Extension Study Shows Safety, Efficacy of rVIII-SingleChain for Previously Treated Hemophilia A
Researchers sought to determine whether rVIII-SingleChain therapy would be safe and effective as a long-term prophylaxis option for previously treated patients with hemophilia A.
PRO Tool, GOAL-Hēm, Now More Patient-Centric for Patients With Hemophilia
Researchers sought to revise the GOAL-Hēm patient-reported outcomes tool to be more patient-centric for patients with hemophilia.
Efanesoctocog Alfa Appears Effective in Severe Hemophilia A
Researchers sought to determine whether efanesoctocog alfa may yield high sustained FVIII activity and improve bleed protection in patients with severe hemophilia A.
Valoctocogene Roxaparvovec Evaluated in Severe Hemophilia A
In open-label study, substantial increase seen in factor VIII activity at weeks 49 to 52 of follow-up.
Gene Therapy Gets Fast Track Status for Hemophilia A
In preclinical studies, ASC618 has been shown to have at least a 10-fold increase in the biosynthesis and secretion of FVIII compared with native human FVIII bioengineered constructs.
Reduced Cardiovascular Morbidity Seen in Patients With Hemophilia
Researchers sought to determine the incidence of fatal and nonfatal CVD during 5 years of follow up in adults with hemophilia.
Millennials With Hemophilia: Attitudes and Expectations From Treatment
Researchers sought to determine the attitudes and expectations of patients with hemophilia belonging to Generation Y regarding their treatment.
Perspectives on Participation in Sports in Patients With Hemophilia
Researchers sought to provide perspectives and recommendations for engaging patients with hemophilia in physical activity.
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