Addressing Barriers to the Use of Gene Therapies and CAR-T Therapies
Researchers sought to determine factors limiting access to gene and CAR-T therapies for patients with hematologic disorders.
Diagnosis & Disease Information
Ibrutinib Plus Rituximab Is Superior to FCR in Previously Untreated CLL
Patients were randomly assigned (1:1) to receive either 6 cycles of FCR every 28 days or IR for up to 6 years.
Vienna Prediction Model Identifies Patients With Unprovoked Venous Thromboembolism Who Are at Low Risk of Recurrence
Researchers sought to create a prediction model to identify patients with unprovoked venous thromboembolism who are at low risk of recurrence.
COVID-19 Vaccination Safe, Effective for Transfusion-Dependent Patients With Beta-Thalassemia
Researchers sought to determine whether the COVID-19 mRNA vaccines were safe and effective in patients with transfusion-dependent beta-thalassemia.
Educational Burdens for Children With Sickle Cell Disease in the US Vs Other Nations
Researchers sought to determine the educational burdens of children with SCD in the US compared with other nations.
Outcomes in Nontransfusion-Dependent β-Thalassemia With Luspatercept or Placebo
Researchers sought to determine whether luspatercept would improve outcomes in patients with nontransfusion-dependent β-thalassemia.
Pegcetacoplan Improves Outcomes Compared With Standard of Care in Patients With Paroxysmal Nocturnal Hemoglobinuria
Researchers sought to determine whether pegcetacoplan would be better than standard of care for treating patients with PNH.
Adding Elotuzumab to Myeloma Treatment Regimens Does Not Improve Outcomes
Predictors of worse progression-free survival included ISS stage II, ISS stage III, and adverse cytogenetics.
Fitusiran Prophylaxis Improves Annualized Bleeding Rate in Hemophilia A and B
Researchers sought to determine whether fitusiran prophylaxis would reduce the rate of bleeding events among patients with hemophilia A or B with inhibitors.
Clonal Hematopoiesis of Indeterminate Potential Associated With Reduced Risk of Alzheimer’s Disease
Researchers sought to determine whether there was an association between the presence of clonal hematopoiesis of indeterminate potential and protection from Alzheimer’s disease.
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