Researchers sought to determine whether prophylactic bolus dosing of tranexamic acid would be similar to continuous infusion in thrombocytopenic patients with hematological disorders.
Researchers sought to determine the risk of transmission of potentially transduction-competent encapsidated vector DNA from valoctocogene roxaparvovec gene therapy for severe hemophilia A.
Researchers sought to determine whether eptacog beta would be an effective treatment for spontaneous and traumatic bleeding events in patients with hemophilia.
Researchers sought to determine whether chronic blood transfusion plays a role in regulating endothelial cell quiescence in pediatric patients with SCA.