Researchers sought to determine the effect of transplant-related complications and socioeconomic factors on revaccination schedule adherence among pediatric patients following allo-HSCT.
Researchers sought to determine whether tisagenlecleucel is safe and effective in patients younger than 3 years old with relapsed/refractory ALL.
Researchers sought to evaluate the effect of the CDC’s guideline on opioid prescriptions and health outcomes on patients with SCD.
Researchers sought to determine whether monitoring SAA levels would be a helpful strategy for determining therapy efficacy in infants with ALL.
Researchers sought to determine whether emicizumab would be safe and effective in pediatric patients with hemophilia A with FVIII inhibitors.
Researchers sought to determine the incidence and impact of food insecurity of pediatric patients with sickle cell disease.
Researchers sought to determine whether intravenous use of ferric carboxymaltose would be a safe and effective treatment option in pediatric patients with iron-deficiency anemia.
Researchers sought to determine risk factors for graft rejection in pediatric patients receiving hematopoietic stem cell transplantation for bone marrow failure.
Researchers sought to determine whether human fibrinogen concentrate would have favorable pharmacokinetics for adult, adolescent, and pediatric patients with congenital fibrinogen deficiency.
Researchers sought to investigate the associations between PTSS and the experiences of pediatric survivors of Hodgkin lymphoma treated in the AHOD0031 study.
Researchers sought to determine whether next generation sequencing may be a helpful tool to detect actionable variants to provide targeted therapies for patients with vascular anomalies.
Researchers sought to determine the safety and efficacy of long-term deferiprone in iron-overloaded patients with sickle cell disease.
Researchers sought to determine the long-term safety and efficacy of KTE-X19 in pediatric and adolescent patients with relapsed or refractory B-cell acute lymphoblastic leukemia.
Researchers sought to determine whether ketorolac dosage could predict the risk of acute kidney injury in pediatric patient with sickle cell disease presenting with a vaso-occlusive pain episode.
Researchers sought to determine whether using azacitidine would be safe for infants with ALL with a KMT2A rearrangement.
Researchers sought to understand how communication breakdowns occur between healthcare providers and parents of children with cancer, and how these can be improved.
Researchers sought to update and assess the interim efficacy, futility, and safety in the phase 3 SPARKLE trial.
Researchers sought to identify and analyze risk factors for thrombosis in adolescent girls receiving hormonal therapy.
Researchers sought to determine whether thromboprophylaxis may help treat patients with POTS to reduce CVC-related thrombosis.
Researchers sought to determine whether deferiprone would have the safe efficacy as deferoxamine for treating iron-overloaded patients with sickle cell disease or other transfusion-dependent anemias.